Sufferers of rare genetic blood disease plead with NHS for ‘life-changing’ US gene therapy

In studies, the one-off transfusion of Zynteglo freed nine in ten patients who had thalassaemia from the twice-monthly blood transfusions they needed to survive.In studies, the one-off transfusion of Zynteglo freed nine in ten patients who had thalassaemia from the twice-monthly blood transfusions they needed to survive.Read MoreHealth News | Mail Online